Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease.
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Curr Gene Ther. 2015;15(1):64-81. doi: 10.2174/1566523214666141127095336.
Curr Gene Ther. 2015.
PMID: 25429463
Free PMC article.