H3B-8800, an orally available small-molecule splicing modulator, induces lethality in spliceosome-mutant cancers.
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Nat Med. 2018 May;24(4):497-504. doi: 10.1038/nm.4493. Epub 2018 Feb 19.
Nat Med. 2018.
PMID: 29457796
Free PMC article.