A Mild PUM1 Mutation Is Associated with Adult-Onset Ataxia, whereas Haploinsufficiency Causes Developmental Delay and Seizures.
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Gennarino VA, et al. Among authors: cowley mj.
Cell. 2018 Feb 22;172(5):924-936.e11. doi: 10.1016/j.cell.2018.02.006.
Cell. 2018.
PMID: 29474920
Free PMC article.