White JW - Search Results

1

Optimized Adeno-Associated Viral-Mediated Human Factor VIII Gene Therapy in Cynomolgus Macaques.

Greig JA, Nordin JML, White JW, Wang Q, Bote E, Goode T, Calcedo R, Wadsworth S, Wang L, Wilson JM. Greig JA, et al. Among authors: white jw. Hum Gene Ther. 2018 Jul 23. doi: 10.1089/hum.2018.080. Online ahead of print. Hum Gene Ther. 2018. PMID: 29890905

2

A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice.

Yang Y, Wang L, Bell P, McMenamin D, He Z, White J, Yu H, Xu C, Morizono H, Musunuru K, Batshaw ML, Wilson JM. Yang Y, et al. Nat Biotechnol. 2016 Mar;34(3):334-8. doi: 10.1038/nbt.3469. Epub 2016 Feb 1. Nat Biotechnol. 2016. PMID: 26829317 Free PMC article.

3

Effects of Self-Complementarity, Codon Optimization, Transgene, and Dose on Liver Transduction with AAV8.

Bell P, Wang L, Chen SJ, Yu H, Zhu Y, Nayal M, He Z, White J, Lebel-Hagan D, Wilson JM. Bell P, et al. Hum Gene Ther Methods. 2016 Dec;27(6):228-237. doi: 10.1089/hgtb.2016.039. Hum Gene Ther Methods. 2016. PMID: 27903094 Free PMC article.

4

AAV gene therapy corrects OTC deficiency and prevents liver fibrosis in aged OTC-knock out heterozygous mice.

Wang L, Bell P, Morizono H, He Z, Pumbo E, Yu H, White J, Batshaw ML, Wilson JM. Wang L, et al. Mol Genet Metab. 2017 Apr;120(4):299-305. doi: 10.1016/j.ymgme.2017.02.011. Epub 2017 Mar 2. Mol Genet Metab. 2017. PMID: 28283349 Free PMC article.

5

Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol.

Wang L, Smith J, Breton C, Clark P, Zhang J, Ying L, Che Y, Lape J, Bell P, Calcedo R, Buza EL, Saveliev A, Bartsevich VV, He Z, White J, Li M, Jantz D, Wilson JM. Wang L, et al. Nat Biotechnol. 2018 Sep;36(8):717-725. doi: 10.1038/nbt.4182. Epub 2018 Jul 9. Nat Biotechnol. 2018. PMID: 29985478

6

CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice.

Wang L, Yang Y, Breton CA, White J, Zhang J, Che Y, Saveliev A, McMenamin D, He Z, Latshaw C, Li M, Wilson JM. Wang L, et al. Blood. 2019 Jun 27;133(26):2745-2752. doi: 10.1182/blood.2019000790. Epub 2019 Apr 11. Blood. 2019. PMID: 30975639 Free article.

7

A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency.

Wang L, Yang Y, Breton C, Bell P, Li M, Zhang J, Che Y, Saveliev A, He Z, White J, Latshaw C, Xu C, McMenamin D, Yu H, Morizono H, Batshaw ML, Wilson JM. Wang L, et al. Sci Adv. 2020 Feb 12;6(7):eaax5701. doi: 10.1126/sciadv.aax5701. eCollection 2020 Feb. Sci Adv. 2020. PMID: 32095520 Free PMC article.

8

Long-term stable reduction of low-density lipoprotein in nonhuman primates following in vivo genome editing of PCSK9.

Wang L, Breton C, Warzecha CC, Bell P, Yan H, He Z, White J, Zhu Y, Li M, Buza EL, Jantz D, Wilson JM. Wang L, et al. Mol Ther. 2021 Jun 2;29(6):2019-2029. doi: 10.1016/j.ymthe.2021.02.020. Epub 2021 Feb 18. Mol Ther. 2021. PMID: 33609733 Free PMC article.

9

Integrated vector genomes may contribute to long-term expression in primate liver after AAV administration.

Greig JA, Martins KM, Breton C, Lamontagne RJ, Zhu Y, He Z, White J, Zhu JX, Chichester JA, Zheng Q, Zhang Z, Bell P, Wang L, Wilson JM. Greig JA, et al. Nat Biotechnol. 2024 Aug;42(8):1232-1242. doi: 10.1038/s41587-023-01974-7. Epub 2023 Nov 6. Nat Biotechnol. 2024. PMID: 37932420 Free PMC article.

10

Thoughtful data analysis.

Bradley E, White JWC, Garland J. Bradley E, et al. Among authors: white jwc. Chaos. 2024 Oct 1;34(10):101502. doi: 10.1063/5.0230739. Chaos. 2024. PMID: 39476013

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Article Language

Species

Sex

Age

Other

326 results

Search Page

Filters