Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device.
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Mol Ther Methods Clin Dev. 2021 Nov 3;23:551-566. doi: 10.1016/j.omtm.2021.10.015. eCollection 2021 Dec 10.
Mol Ther Methods Clin Dev. 2021.
PMID: 34853801
Free PMC article.