A Combined Prospective and Retrospective Comparison of Long-Term Functional Outcomes Suggests Delayed Loss of Ambulation and Pulmonary Decline with Long-Term Eteplirsen Treatment.
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Mitelman O, et al. Among authors: santra s.
J Neuromuscul Dis. 2022;9(1):39-52. doi: 10.3233/JND-210665.
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PMID: 34420980
Free PMC article.
Clinical Trial.