Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function.
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Neurology. 2019 Sep 24;93(13):e1312-e1323. doi: 10.1212/WNL.0000000000008168. Epub 2019 Aug 26.
Neurology. 2019.
PMID: 31451516
Free PMC article.
Clinical Trial.