Targeted exon skipping of NF1 exon 17 as a therapeutic for neurofibromatosis type I.
Leier A, Moore M, Liu H, Daniel M, Hyde AM, Messiaen L, Korf BR, Selvakumaran J, Ciszewski L, Lambert L, Foote J, Wallace MR, Kesterson RA, Dickson G, Popplewell L, Wallis D.
Leier A, et al. Among authors: liu h.
Mol Ther Nucleic Acids. 2022 Mar 15;28:261-278. doi: 10.1016/j.omtn.2022.03.011. eCollection 2022 Jun 14.
Mol Ther Nucleic Acids. 2022.
PMID: 35433111
Free PMC article.