Biallelic PI4KA variants cause a novel neurodevelopmental syndrome with hypomyelinating leukodystrophy.
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Verdura E, et al. Among authors: mandrile g.
Brain. 2021 Oct 22;144(9):2659-2669. doi: 10.1093/brain/awab124.
Brain. 2021.
PMID: 34415322
Free PMC article.