Microvasculopathy in spinal muscular atrophy is driven by a reversible autonomous endothelial cell defect.
Zhou H, Hong Y, Scoto M, Thomson A, Pead E, MacGillivray T, Hernandez-Gerez E, Catapano F, Meng J, Zhang Q, Hunter G, Shorrock HK, Ng TK, Hamida A, Sanson M, Baranello G, Howell K, Gillingwater TH, Brogan P, Thompson DA, Parson SH, Muntoni F.
Zhou H, et al. Among authors: pead e.
J Clin Invest. 2022 Nov 1;132(21):e153430. doi: 10.1172/JCI153430.
J Clin Invest. 2022.
PMID: 36099045
Free PMC article.