Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models.
Song Y, Morales L, Malik AS, Mead AF, Greer CD, Mitchell MA, Petrov MT, Su LT, Choi ME, Rosenblum ST, Lu X, VanBelzen DJ, Krishnankutty RK, Balzer FJ, Loro E, French R, Propert KJ, Zhou S, Kozyak BW, Nghiem PP, Khurana TS, Kornegay JN, Stedman HH.
Song Y, et al. Among authors: mitchell ma.
Nat Med. 2019 Oct;25(10):1505-1511. doi: 10.1038/s41591-019-0594-0. Epub 2019 Oct 7.
Nat Med. 2019.
PMID: 31591596
Free PMC article.