Phase II/III Study of Aceneuramic Acid Administration for GNE Myopathy in Japan.
Suzuki N, Mori-Yoshimura M, Katsuno M, Takahashi MP, Yamashita S, Oya Y, Hashizume A, Yamada S, Nakamori M, Izumi R, Kato M, Warita H, Tateyama M, Kuroda H, Asada R, Yamaguchi T, Nishino I, Aoki M.
Suzuki N, et al. Among authors: hashizume a.
J Neuromuscul Dis. 2023;10(4):555-566. doi: 10.3233/JND-230029.
J Neuromuscul Dis. 2023.
PMID: 37125562
Free PMC article.
Clinical Trial.