Targeted genome editing in vivo corrects a Dmd duplication restoring wild-type dystrophin expression.
Maino E, Wojtal D, Evagelou SL, Farheen A, Wong TWY, Lindsay K, Scott O, Rizvi SZ, Hyatt E, Rok M, Visuvanathan S, Chiodo A, Schneeweiss M, Ivakine EA, Cohn RD.
Maino E, et al. Among authors: ivakine ea.
EMBO Mol Med. 2021 May 7;13(5):e13228. doi: 10.15252/emmm.202013228. Epub 2021 Mar 16.
EMBO Mol Med. 2021.
PMID: 33724658
Free PMC article.