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Page 1
A Comprehensive Map of CNS Transduction by Eight Recombinant Adeno-associated Virus Serotypes Upon Cerebrospinal Fluid Administration in Pigs.
Sorrentino NC, Maffia V, Strollo S, Cacace V, Romagnoli N, Manfredi A, Ventrella D, Dondi F, Barone F, Giunti M, Graham AR, Huang Y, Kalled SL, Auricchio A, Bacci ML, Surace EM, Fraldi A. Sorrentino NC, et al. Among authors: cacace v. Mol Ther. 2016 Feb;24(2):276-286. doi: 10.1038/mt.2015.212. Epub 2015 Dec 7. Mol Ther. 2016. PMID: 26639405 Free PMC article.
Enhancing the Therapeutic Potential of Sulfamidase for the Treatment of Mucopolysaccharidosis IIIA.
Sorrentino NC, Cacace V, De Risi M, Maffia V, Strollo S, Tedesco N, Nusco E, Romagnoli N, Ventrella D, Huang Y, Liu N, Kalled SL, Choi VW, De Leonibus E, Fraldi A. Sorrentino NC, et al. Among authors: cacace v. Mol Ther Methods Clin Dev. 2019 Oct 28;15:333-342. doi: 10.1016/j.omtm.2019.10.009. eCollection 2019 Dec 13. Mol Ther Methods Clin Dev. 2019. PMID: 31788497 Free PMC article.
Fluoxetine ameliorates mucopolysaccharidosis type IIIA.
Capuozzo A, Montefusco S, Cacace V, Sofia M, Esposito A, Napolitano G, Nusco E, Polishchuk E, Pizzo MT, De Risi M, De Leonibus E, Sorrentino NC, Medina DL. Capuozzo A, et al. Among authors: cacace v. Mol Ther. 2022 Apr 6;30(4):1432-1450. doi: 10.1016/j.ymthe.2022.01.037. Epub 2022 Feb 2. Mol Ther. 2022. PMID: 35121108 Free PMC article.
The Amyloid Inhibitor CLR01 Relieves Autophagy and Ameliorates Neuropathology in a Severe Lysosomal Storage Disease.
Monaco A, Maffia V, Sorrentino NC, Sambri I, Ezhova Y, Giuliano T, Cacace V, Nusco E, De Risi M, De Leonibus E, Schrader T, Klärner FG, Bitan G, Fraldi A. Monaco A, et al. Among authors: cacace v. Mol Ther. 2022 Nov 2;30(11):3499. doi: 10.1016/j.ymthe.2022.10.001. Epub 2022 Oct 18. Mol Ther. 2022. PMID: 36261045 Free PMC article. No abstract available.
New mouse models with hypomorphic SUMF1 variants mimic attenuated forms of multiple sulfatase deficiency.
Sorrentino NC, Presa M, Attanasio S, Cacace V, Sofia M, Zuberi A, Ryan J, Ray S, Petkovic I, Radhakrishnan K, Schlotawa L, Ballabio A, Lutz C, Brunetti-Pierri N. Sorrentino NC, et al. Among authors: cacace v. J Inherit Metab Dis. 2023 Mar;46(2):335-347. doi: 10.1002/jimd.12577. Epub 2022 Dec 11. J Inherit Metab Dis. 2023. PMID: 36433920 Free PMC article.
The molecular causes of thyroid dysgenesis: a systematic review.
Nettore IC, Cacace V, De Fusco C, Colao A, Macchia PE. Nettore IC, et al. Among authors: cacace v. J Endocrinol Invest. 2013 Sep;36(8):654-64. doi: 10.3275/8973. Epub 2013 May 22. J Endocrinol Invest. 2013. PMID: 23698639 Review.
19 results