Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device.
Olgasi C, Borsotti C, Merlin S, Bergmann T, Bittorf P, Adewoye AB, Wragg N, Patterson K, Calabria A, Benedicenti F, Cucci A, Borchiellini A, Pollio B, Montini E, Mazzuca DM, Zierau M, Stolzing A, Toleikis PM, Braspenning J, Follenzi A.
Olgasi C, et al. Among authors: borsotti c.
Mol Ther Methods Clin Dev. 2021 Nov 3;23:551-566. doi: 10.1016/j.omtm.2021.10.015. eCollection 2021 Dec 10.
Mol Ther Methods Clin Dev. 2021.
PMID: 34853801
Free PMC article.