CRISPR-targeted MAGT1 insertion restores XMEN patient hematopoietic stem cells and lymphocytes.
Brault J, Liu T, Bello E, Liu S, Sweeney CL, Meis RJ, Koontz S, Corsino C, Choi U, Vayssiere G, Bosticardo M, Dowdell K, Lazzarotto CR, Clark AB, Notarangelo LD, Ravell JC, Lenardo MJ, Kleinstiver BP, Tsai SQ, Wu X, Dahl GA, Malech HL, De Ravin SS.
Brault J, et al. Among authors: liu s, liu t.
Blood. 2021 Dec 30;138(26):2768-2780. doi: 10.1182/blood.2021011192.
Blood. 2021.
PMID: 34086870
Free PMC article.