Self-complementary AAV-mediated gene therapy restores cone function and prevents cone degeneration in two models of Rpe65 deficiency.
Pang J, Boye SE, Lei B, Boye SL, Everhart D, Ryals R, Umino Y, Rohrer B, Alexander J, Li J, Dai X, Li Q, Chang B, Barlow R, Hauswirth WW.
Pang J, et al. Among authors: boye sl, boye se.
Gene Ther. 2010 Jul;17(7):815-26. doi: 10.1038/gt.2010.29. Epub 2010 Mar 18.
Gene Ther. 2010.
PMID: 20237510
Free PMC article.