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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1969 1
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1978 2
1982 1
1983 1
1984 2
1988 1
1989 2
1990 1
1992 2
1993 1
1994 1
1995 1
1996 3
1997 1
1998 4
1999 6
2000 3
2001 2
2002 11
2003 2
2004 5
2005 7
2006 5
2007 6
2008 9
2009 13
2010 9
2011 13
2012 17
2013 14
2014 11
2015 17
2016 19
2017 14
2018 11
2019 19
2020 12
2021 18
2022 15
2023 18
2024 24
2025 0

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289 results

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Page 1
Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Among authors: byrne bj. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.
Current avenues of gene therapy in Pompe disease.
Leon-Astudillo C, Trivedi PD, Sun RC, Gentry MS, Fuller DD, Byrne BJ, Corti M. Leon-Astudillo C, et al. Among authors: byrne bj. Curr Opin Neurol. 2023 Oct 1;36(5):464-473. doi: 10.1097/WCO.0000000000001187. Epub 2023 Jul 19. Curr Opin Neurol. 2023. PMID: 37639402 Free PMC article. Review.
Pompe disease diagnosis and management guideline.
Kishnani PS, Steiner RD, Bali D, Berger K, Byrne BJ, Case LE, Crowley JF, Downs S, Howell RR, Kravitz RM, Mackey J, Marsden D, Martins AM, Millington DS, Nicolino M, O'Grady G, Patterson MC, Rapoport DM, Slonim A, Spencer CT, Tifft CJ, Watson MS. Kishnani PS, et al. Among authors: byrne bj. Genet Med. 2006 May;8(5):267-88. doi: 10.1097/01.gim.0000218152.87434.f3. Genet Med. 2006. PMID: 16702877 Free PMC article. No abstract available.
Eteplirsen for the treatment of Duchenne muscular dystrophy.
Mendell JR, Rodino-Klapac LR, Sahenk Z, Roush K, Bird L, Lowes LP, Alfano L, Gomez AM, Lewis S, Kota J, Malik V, Shontz K, Walker CM, Flanigan KM, Corridore M, Kean JR, Allen HD, Shilling C, Melia KR, Sazani P, Saoud JB, Kaye EM; Eteplirsen Study Group. Mendell JR, et al. Ann Neurol. 2013 Nov;74(5):637-47. doi: 10.1002/ana.23982. Epub 2013 Sep 10. Ann Neurol. 2013. PMID: 23907995 Free article. Clinical Trial.
Nicholas Muzyczka, PhD.
Berns KI, Byrne BJ, Flotte TR, Samulski RJ, Srivastava A. Berns KI, et al. Among authors: byrne bj. Mol Ther. 2023 Mar 1;31(3):607. doi: 10.1016/j.ymthe.2023.01.027. Epub 2023 Feb 10. Mol Ther. 2023. PMID: 36764298 Free PMC article. No abstract available.
Neonatal outreach simulation.
Byrne BJ, Manhas D. Byrne BJ, et al. Semin Perinatol. 2016 Nov;40(7):480-488. doi: 10.1053/j.semperi.2016.08.009. Epub 2016 Sep 28. Semin Perinatol. 2016. PMID: 27692476 Review.
289 results