alpha-thalassemia resulting from a negative chromosomal position effect

Blood. 2000 Aug 1;96(3):800-7.

Abstract

To date, all of the chromosomal deletions that cause alpha-thalassemia remove the structural alpha genes and/or their regulatory element (HS -40). A unique deletion occurs in a single family that juxtaposes a region that normally lies approximately 18-kilobase downstream of the human alpha cluster, next to a structurally normal alpha-globin gene, and silences its expression. During development, the CpG island associated with the alpha-globin promoter in the rearranged chromosome becomes densely methylated and insensitive to endonucleases, demonstrating that the normal chromatin structure around the alpha-globin gene is perturbed by this mutation and that the gene is inactivated by a negative chromosomal position effect. These findings highlight the importance of the chromosomal environment in regulating globin gene expression.

MeSH terms

  • Chromosome Mapping
  • Chromosomes, Human, Pair 16*
  • DNA Methylation
  • Globins / genetics
  • Humans
  • Sequence Deletion*
  • alpha-Thalassemia / etiology
  • alpha-Thalassemia / genetics*

Substances

  • Globins