A novel strategy for cancer therapy by mutated mammalian degenerin gene transfer

Cancer Gene Ther. 2000 Oct;7(10):1341-7. doi: 10.1038/sj.cgt.7700249.

Abstract

Mammalian degenerin (MDEG) is a member of the amiloride-sensitive sodium ion channel family, and its site-directed active mutant (MDEG-G430F) induces massive Na+ influx into cells, leading to cell ballooning and cell bursting. We attempted a novel therapeutic approach for gastric cancers by transferring MDEG-G430F into cancer cells using tumor-specific promoters. In carcinoembryonic antigen (CEA)-producing gastric cancer cells, the level of cell death observed when MDEG-G430F was used with a CEA promoter was similar to that observed when using a potent nonspecific promoter such as the cytomegalovirus promoter. In an in vivo study, fusogenic liposome complexes containing MDEG-G430F driven by the CEA promoter were injected intraperitoneally into CEA-producing gastric cancer cells in a mouse peritoneal dissemination model. Although all 15 of the control mice were dead by 50 days postinoculation, 13 of the 15 mice treated with MDEG-G430F survived. These results indicate that transferring MDEG-G430F into cancer tissues using tumor-specific promoters can achieve striking and selective cancer cell death irrespective of the transcriptional efficiency of the promoters used in vivo, and suggest that this approach is a promising new strategy for cancer gene therapy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acid Sensing Ion Channels
  • Animals
  • Carcinoembryonic Antigen / biosynthesis
  • Carcinoembryonic Antigen / genetics*
  • Cell Survival / drug effects
  • Degenerin Sodium Channels
  • Epithelial Sodium Channels
  • Female
  • Humans
  • Injections, Intraperitoneal
  • Ion Channels / genetics*
  • Ion Channels / metabolism
  • Ion Channels / therapeutic use*
  • Liposomes
  • Liver Neoplasms / metabolism
  • Liver Neoplasms / therapy*
  • Luciferases / metabolism
  • Mice
  • Mice, Inbred BALB C
  • Mice, Nude
  • Mutagenesis, Site-Directed / genetics*
  • Mutation / genetics*
  • Neoplasm Transplantation
  • Nerve Tissue Proteins / genetics*
  • Nerve Tissue Proteins / metabolism
  • Nerve Tissue Proteins / therapeutic use*
  • Peritoneal Diseases / pathology
  • Stomach Neoplasms / therapy*
  • Survival Rate
  • Time Factors
  • Transduction, Genetic / methods*
  • Tumor Cells, Cultured

Substances

  • ASIC2 protein, human
  • Acid Sensing Ion Channels
  • Carcinoembryonic Antigen
  • Degenerin Sodium Channels
  • Epithelial Sodium Channels
  • Ion Channels
  • Liposomes
  • Nerve Tissue Proteins
  • Luciferases