Congenital dyserythropoietic anemia type 1 with fetal onset of severe anemia

J Pediatr Hematol Oncol. 2001 Jan;23(1):63-6. doi: 10.1097/00043426-200101000-00016.

Abstract

We report a patient with congenital dyserythropoietic anemia type 1 with characteristic anomalies and two novel clinicopathologic presentations: intrauterine onset of severe anemia resulting in cardiac failure and relatively mild dyserythropoietic features on bone marrow aspiration in contrast to severity of anemia. After repeated transfusions and a trial of erythropoietin administration, the patient died from respiratory infection at age 7 months. Autopsy revealed characteristic dyserythropoietic features of the bone marrow by light microscopy and electron microscopy, which confirmed a diagnosis of congenital dyserythropoietic anemia type 1.

Publication types

  • Case Reports

MeSH terms

  • Anemia, Dyserythropoietic, Congenital / diagnosis*
  • Anemia, Dyserythropoietic, Congenital / embryology
  • Anemia, Dyserythropoietic, Congenital / therapy
  • Blood Transfusion
  • Erythroblasts / pathology
  • Erythroblasts / ultrastructure
  • Erythropoietin / therapeutic use
  • Fatal Outcome
  • Female
  • Humans
  • Infant, Newborn
  • Recombinant Proteins

Substances

  • Recombinant Proteins
  • Erythropoietin