Congenital ovine neuronal ceroid lipofuscinosis--a cathepsin D deficiency with increased levels of the inactive enzyme

Eur J Paediatr Neurol. 2001:5 Suppl A:43-5. doi: 10.1053/ejpn.2000.0433.

Abstract

We recently showed that a form of neuronal ceroid lipofuscinosis (NCL) in white Swedish landrace sheep is caused by a missense mutation in the cathepsin D gene resulting in complete inactivation of the enzyme. Despite the lack of cathepsin D activity, the brains of the cathepsin D deficient sheep showed strongly increased staining for cathepsin D in immunohistochemistry. By Western blotting, a 5-10 fold increase in the level of cathepsin D was confirmed. These results indicate that the missense mutation in congenital NCL sheep results in the synthesis of an inactive yet stable cathepsin D.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cathepsin D / analysis
  • Cathepsin D / deficiency*
  • Cathepsin D / genetics
  • Frontal Lobe / enzymology
  • Lysosomes / enzymology
  • Mutation, Missense
  • Nerve Degeneration / congenital
  • Nerve Degeneration / enzymology
  • Neuronal Ceroid-Lipofuscinoses / congenital
  • Neuronal Ceroid-Lipofuscinoses / enzymology*
  • Sheep

Substances

  • Cathepsin D