Right ventricular gene therapy with a beta-adrenergic receptor kinase inhibitor improves survival after pulmonary artery banding

Ann Thorac Surg. 2001 Nov;72(5):1657-61. doi: 10.1016/s0003-4975(01)03130-7.

Abstract

Background: Increased right ventricular (RV) afterload results in RV hypertrophy and dysfunction, as well as increased levels of intracellular beta-adrenergic receptor kinase (betaARK1). We hypothesize that gene transfer of a betaARK1 inhibitor (betaARKct) may improve RV performance, morbidity, and mortality early after pulmonary artery (PA) banding.

Methods: Rabbits underwent PA banding 3 days after right coronary artery injection of an adenovirus containing the gene encoding the betaARKct peptide (n = 14), beta-galactosidase (n = 10), or an empty adenovirus (n = 19). After banding, hemodynamic instability and maximal rate of increase in right ventricular pressure (RV dP/dt(max)) were documented. For 7 days after banding, animals were monitored for mortality, activity, and appetite.

Results: When compared with controls, animals receiving the betaARKct transgene showed improvement in survival at 7 days (92.8% +/- 7% vs 48.3% +/- 9%, p = 0.01), less lethargy, a trend toward greater RV dP/dt(max) (NS), and increased hemodynamic stability at the time of banding (78% vs 41%, p = 0.03).

Conclusions: Selective RV expression of betaARKct improves survival and morbidity after PA banding. This represents a novel therapeutic modality for clinical situations involving increased RV afterload.

MeSH terms

  • Animals
  • Carrier Proteins / therapeutic use*
  • Genetic Therapy / methods*
  • Heart Ventricles*
  • Peptides*
  • Pulmonary Artery*
  • Rabbits
  • Recombinant Proteins*
  • Survival Rate
  • Transgenes
  • Ventricular Dysfunction, Right / mortality
  • Ventricular Dysfunction, Right / pathology
  • Ventricular Dysfunction, Right / therapy*

Substances

  • Carrier Proteins
  • Peptides
  • Recombinant Proteins
  • beta-adrenergic receptor kinase inhibitory peptide