Delta ribozyme benefits from a good stability in vitro that becomes outstanding in vivo

RNA. 2002 Apr;8(4):464-77. doi: 10.1017/s1355838202020289.

Abstract

The stability of a trans-acting delta ribozyme was studied under various conditions. Although in vitro (i.e., in the presence of protein extracts) this delta ribozyme appears to be only slightly more stable than a hammerhead ribozyme, in vivo (i.e., after cell transfection) it exhibits an outstanding stability that manifests itself in the calculated half-life of over 100 h regardless of the means of transfection. The P2 stem, which includes both the 5' and 3' ends, is shown to play a critical role in this stability. Direct mutagenesis of the most nuclease susceptible nucleotides failed to generate a more stable ribozyme that retained the same catalytic potential. Clearly, delta ribozyme appears to be well adapted to the human cell environment, and is therefore ideal for the development of a gene-inactivation system.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Base Sequence
  • Catalytic Domain
  • Cells, Cultured
  • Hepatitis Delta Virus / genetics
  • Humans
  • Molecular Sequence Data
  • Mutagenesis
  • RNA Stability
  • RNA, Catalytic / chemistry*
  • RNA, Catalytic / metabolism*
  • Structure-Activity Relationship

Substances

  • RNA, Catalytic