Maturity-onset diabetes of the young resulting from a novel mutation in the HNF-4alpha gene

Intern Med. 2002 Oct;41(10):848-52. doi: 10.2169/internalmedicine.41.848.

Abstract

A 52-year-old woman with early-onset diabetes mellitus, severe diabetic retinopathy, and a family history of a dominant inheritance pattern was referred to our hospital. Direct sequencing revealed a novel mutation in the HNF-4alpha gene (R244Q). The position of the mutation in the amino-acid sequence of the gene is well conserved among species and transcriptional activity of the mutant gene was significantly reduced. Therefore, a diagnosis of maturity-onset diabetes of the young (MODY)-1 was made. Genetic testing enabled early diagnosis of diabetes in the patient's 20-year-old daughter, which we consider to be important for the prevention of diabetic complications.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Age of Onset
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors
  • Blood Glucose / analysis
  • DNA-Binding Proteins / genetics
  • Diabetes Mellitus, Type 2 / genetics*
  • Diabetes Mellitus, Type 2 / physiopathology
  • Female
  • Genes, Dominant / genetics
  • Glucose Tolerance Test
  • Hepatocyte Nuclear Factor 4
  • Humans
  • Middle Aged
  • Mutation*
  • Pedigree
  • Phosphoproteins / genetics*
  • Transcription Factors / genetics*
  • Transcription, Genetic / physiology

Substances

  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors
  • Blood Glucose
  • DNA-Binding Proteins
  • HNF4A protein, human
  • Hepatocyte Nuclear Factor 4
  • MLX protein, human
  • Phosphoproteins
  • Transcription Factors