Abstract
An X-linked creatine deficiency syndrome caused by mutations in the creatine transporter gene SLC6A8/CRTR mapped to Xq28 has recently been described. Essential in the recognition of this disorder is the absence of creatine on proton magnetic resonance spectroscopy (MRS) examination. A 9-day-old heterozygous female child with this syndrome demonstrated a significant reduction of creatine on proton MRS. She is a carrier of the R514X nonsense mutation.
MeSH terms
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Amino Acid Metabolism, Inborn Errors / diagnosis*
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Amino Acid Metabolism, Inborn Errors / metabolism
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Amino Acid Metabolism, Inborn Errors / pathology
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Brain / pathology
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Brain Chemistry*
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Codon, Nonsense
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Creatine / analysis
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Creatine / deficiency*
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Creatine / genetics
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Female
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Genetic Diseases, X-Linked / diagnosis*
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Genetic Diseases, X-Linked / pathology
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Heterozygote*
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Humans
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Infant, Newborn
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Magnetic Resonance Spectroscopy*
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Membrane Transport Proteins / deficiency*
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Membrane Transport Proteins / genetics*
Substances
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Codon, Nonsense
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Membrane Transport Proteins
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creatine transporter
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Creatine