Mithramycin SK, a novel antitumor drug with improved therapeutic index, mithramycin SA, and demycarosyl-mithramycin SK: three new products generated in the mithramycin producer Streptomyces argillaceus through combinatorial biosynthesis

J Am Chem Soc. 2003 May 14;125(19):5745-53. doi: 10.1021/ja034162h.

Abstract

To gain initial structure-activity relationships regarding the highly functionalized pentyl side chain attached at C-3 of mithramycin (MTM), we focused on a post-polyketide synthase (post-PKS) tailoring step of the MTM biosynthesis by Streptomyces argillaceus ATCC 12956, which was proposed to be catalyzed by ketoreductase (KR) MtmW. In this last step of the MTM biosynthesis, a keto group of the pentyl side chain is reduced to a secondary alcohol, and we anticipated the generation of an MTM derivative with an additional keto group in the 3-side chain. Insertional inactivation of mtmW, a gene located ca. 8 kb downstream of the mithramycin-PKS genes, yielded an S. argillaceus mutant, which accumulated three new mithramycin analogues, namely mithramycin SA, demycarosyl-mithramycin SK, and mithramycin SK (MTM-SK). The structures of these three compounds confirmed indirectly the proposed role of MtmW in MTM biosynthesis. However, the new mithramycin derivatives bear unexpectedly shorter 3-side chains (ethyl or butyl) than MTM, presumably caused by nonenzymatic rearrangement or cleavage reactions of the initially formed pentyl side chain with a reactive beta-dicarbonyl functional group. The major product, MTM-SK, was tested in vitro against a variety of human cancer cell lines, as well as in an in vitro toxicity assay, and showed an improved therapeutic index, in comparison to the parent drug, MTM.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Antibiotics, Antineoplastic / biosynthesis*
  • Antibiotics, Antineoplastic / pharmacology
  • Carbohydrate Sequence
  • Combinatorial Chemistry Techniques
  • Drug Screening Assays, Antitumor
  • Gene Silencing
  • Humans
  • Molecular Sequence Data
  • Mutagenesis, Insertional
  • Nuclear Magnetic Resonance, Biomolecular / methods
  • Oxidoreductases / genetics
  • Oxidoreductases / metabolism
  • Plicamycin / analogs & derivatives*
  • Plicamycin / biosynthesis
  • Plicamycin / pharmacology
  • Streptomyces / enzymology
  • Streptomyces / genetics
  • Streptomyces / metabolism*
  • Trisaccharides / biosynthesis
  • Trisaccharides / metabolism
  • Tumor Cells, Cultured

Substances

  • Antibiotics, Antineoplastic
  • Trisaccharides
  • Oxidoreductases
  • Plicamycin