Strategy for randomised clinical trials in rare cancers

BMJ. 2003 Jul 5;327(7405):47-9. doi: 10.1136/bmj.327.7405.47.

Abstract

Proving that a new treatment is more effective than current treatment can be difficult for rare conditions. Data from small randomised trials could, however, be made more robust by taking other related research into account

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Data Interpretation, Statistical
  • Humans
  • Neoplasms / therapy*
  • Proportional Hazards Models
  • Randomized Controlled Trials as Topic / methods*
  • Rare Diseases / therapy*
  • Statistical Distributions