Identification of novel mutations in Na-Cl cotransporter gene in a Korean patient with atypical Gitelman's syndrome

Am J Kidney Dis. 2003 Dec;42(6):E11-6. doi: 10.1053/j.ajkd.2003.08.035.

Abstract

The authors report the case of a 20-year-old man with unexplained hypokalemia and metabolic alkalosis suggesting hypokalemic tubulopathy. Interestingly, he showed a mixed phenotype of Gitelman's syndrome (GS) and Bartter's syndrome, which includes normomagnesemia, normal renal magnesium excretion, and hypocalciuria. Renal clearance study showed the presence of a critical defect in the distal nephron rather than loop of Henle. Further family study showed that his mother had a definitive phenotype of GS. By the molecular genetic analysis of these patients, 7 different mutations of the NCCT gene were identified consisting of 3 missense, 1 splice site, and 3 silent mutations. Four of these mutations were novel. The authors emphasize that the combination of a molecular genetic approach and renal clearance study could be of practical benefit in confusing clinical setting and support new diagnostic criteria in GS.

MeSH terms

  • Adult
  • Alkalosis / genetics
  • Amino Acid Substitution
  • Bartter Syndrome / diagnosis
  • Bartter Syndrome / genetics
  • Calcium / urine
  • Carrier Proteins / chemistry
  • Carrier Proteins / genetics*
  • DNA Mutational Analysis
  • Diagnosis, Differential
  • Exons / genetics
  • Female
  • Humans
  • Hypokalemia / genetics
  • Hypokalemic Periodic Paralysis / genetics*
  • Introns / genetics
  • Korea
  • Magnesium / blood
  • Male
  • Mutagenesis, Insertional
  • Mutation*
  • Mutation, Missense
  • Phenotype
  • RNA Splice Sites / genetics
  • Receptors, Drug*
  • Renal Tubular Transport, Inborn Errors / diagnosis
  • Renal Tubular Transport, Inborn Errors / genetics*
  • Renal Tubular Transport, Inborn Errors / metabolism
  • Sodium Chloride Symporters
  • Solute Carrier Family 12, Member 3
  • Symporters*
  • Syndrome

Substances

  • Carrier Proteins
  • RNA Splice Sites
  • Receptors, Drug
  • SLC12A3 protein, human
  • Sodium Chloride Symporters
  • Solute Carrier Family 12, Member 3
  • Symporters
  • thiazide receptor
  • Magnesium
  • Calcium