Molecular characterization of an 11q14.3 microdeletion associated with leukodystrophy

Eur J Hum Genet. 2004 Mar;12(3):245-50. doi: 10.1038/sj.ejhg.5201128.

Abstract

Leukodystrophies represent a heterogeneous group of rare hereditary diseases affecting the central nervous system. The underlying molecular defect remains unknown in almost 50% of cases. We previously assigned a new locus for leukodystrophy of unknown cause to chromosome 11q14.3 by identifying a de novo microdeletion in a sporadic case. We now report the precise molecular characterization of this microdeletion. Physical mapping of the region of interest allowed us to identify and analyze candidate gene(s) possibly implicated in leukodystrophy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cathepsin C / genetics
  • Chromosome Deletion*
  • Chromosomes, Artificial, Bacterial / genetics
  • Chromosomes, Human, Pair 11 / genetics*
  • Contig Mapping
  • Humans
  • In Situ Hybridization, Fluorescence
  • Leukodystrophy, Metachromatic / genetics*
  • Microsatellite Repeats / genetics
  • Physical Chromosome Mapping*
  • Receptor, Metabotropic Glutamate 5
  • Receptors, Metabotropic Glutamate / genetics

Substances

  • Receptor, Metabotropic Glutamate 5
  • Receptors, Metabotropic Glutamate
  • Cathepsin C