Clinical and biochemical aspects of carnitine deficiency and insufficiency: transport defects and inborn errors of beta-oxidation

Crit Rev Clin Lab Sci. 1992;29(3-4):217-42. doi: 10.3109/10408369209114601.

Abstract

Carnitine is required for entry of long chain fatty acids into mitochondria where beta-oxidation occurs. Primary carnitine deficiency, due to a generic defect in cellular carnitine transport, exists in myopathic and systemic forms. Secondary carnitine deficiency may be due to multiplicity of inherited abnormalities, including deficiencies in carnitine palmitoyl-transferase acyl-CoA dehydrogenases, electron transfer flavoprotein, and 3-ketoacyl-CoA-thiolase. The clinical features, diagnosis, and treatment of these conditions are described.

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Biological Transport, Active
  • Carnitine / deficiency*
  • Carnitine / metabolism
  • Fatty Acids / metabolism
  • Humans
  • Metabolism, Inborn Errors / metabolism
  • Mitochondria / metabolism
  • Oxidation-Reduction
  • Vitamin B Deficiency / metabolism*

Substances

  • Fatty Acids
  • Carnitine