Targeting prion amyloid deposits in vivo

J Neuropathol Exp Neurol. 2004 Jul;63(7):775-84. doi: 10.1093/jnen/63.7.775.

Abstract

The diagnosis of prion diseases in humans is challenging due to a lack of specific and sensitive non-invasive tests. Many forms of human prion disease including variant Creutzfeldt-Jakob disease (vCJD), Gerstmann-Sträussler-Scheinker (GSS) syndrome, and 10% of sporadic CJD cases are associated with amyloid deposition. Several positron emission tomography (PET) ligands have recently been developed to directly image beta-amyloid associated with Alzheimer disease. One of them, methoxy-X04, is a fluorescent derivative of Congo red with high binding affinity toward amyloid fibrils and good blood-brain barrier permeability. Using methoxy-X04, we investigated whether amyloid-targeting ligands can be also employed for direct imaging of amyloid deposits associated with some prion diseases. Such a method could potentially become a novel diagnostic approach for these conditions. Studies were performed on MB mice infected with the 87V mouse-adapted scrapie strain. Labeling of PrP amyloid plaques in brains of presymptomatic and symptomatic mice was demonstrated using in vivo transcranial two-photon microscopy after systemic administration of methoxy-X04. During real-time imaging, PrP amyloid deposits could be clearly distinguished 15 min after intravenous administration of methoxy-X04. The ligand showed rapid clearance from brain areas that did not contain amyloid deposits. PrP amyloid deposits could also be detected by direct application of methoxy-X04 on cerebellar sections from GSS patients. These results suggest that methoxy-X04 or similar derivatives could be used as PET imaging agents to improve the diagnosis of human prion diseases associated with amyloid deposition.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Alkenes* / metabolism
  • Alkenes* / pharmacokinetics
  • Amyloid beta-Peptides / analysis*
  • Animals
  • Benzene Derivatives* / metabolism
  • Benzene Derivatives* / pharmacokinetics
  • Brain / metabolism
  • Brain / pathology
  • Disease Models, Animal
  • Humans
  • Metabolic Clearance Rate / drug effects
  • Metabolic Clearance Rate / physiology
  • Mice
  • Plaque, Amyloid / metabolism
  • Plaque, Amyloid / pathology*
  • Predictive Value of Tests
  • Prion Diseases / diagnostic imaging*
  • Prion Diseases / metabolism
  • Prion Diseases / pathology*
  • Reproducibility of Results
  • Scrapie / diagnostic imaging
  • Scrapie / metabolism
  • Scrapie / pathology
  • Stilbenes
  • Tomography, Emission-Computed / methods*

Substances

  • 1,4-bis(4'-hydroxystyryl)-2-methoxybenzene
  • Alkenes
  • Amyloid beta-Peptides
  • Benzene Derivatives
  • Stilbenes