Clinical features of hereditary spinocerebellar ataxia diagnosed by molecular genetic analysis

Hong Kong Med J. 2004 Aug;10(4):255-9.

Abstract

Objective: To assess the frequency and clinical features of different types of hereditary spinocerebellar ataxia in Hong Kong.

Design: Cross-sectional study using a questionnaire and clinical examination, with the majority of the information retrospectively collected.

Setting: Three regional hospitals, Hong Kong.

Participants: All patients with spinocerebellar ataxia that was confirmed by molecular genetic tests between January 2001 and October 2003.

Main outcome measures: History, latest physical examination results, clinical investigation results, and genetic profiles.

Results: A total of 16 Chinese patients had received diagnoses of spinocerebellar ataxia. These patients had spinocerebellar ataxia type 1 (n=3), spinocerebellar ataxia type 3 (Machado-Joseph disease; n=12), and dentatorubro-pallidoluysian atrophy (n=1). The most common manifestation was ataxia (15/16), followed by pyramidal signs (12/16). Other features such as bulbar dysfunction, ophthalmoplegia, neuropathy, and cognitive impairment were present but variable.

Conclusions: The clinical manifestations of different types of spinocerebellar ataxia overlap, and genetic study is necessary to confirm the diagnosis. The frequency of spinocerebellar ataxia type 3 is greater than that of other types among these Chinese patients. The age of onset of this type may correlate inversely with the number of CAG repeats.

Publication types

  • Multicenter Study

MeSH terms

  • Adult
  • Cross-Sectional Studies
  • Female
  • Hong Kong
  • Humans
  • Machado-Joseph Disease / diagnosis*
  • Machado-Joseph Disease / genetics
  • Male
  • Middle Aged
  • Retrospective Studies
  • Spinocerebellar Ataxias / diagnosis*
  • Spinocerebellar Ataxias / genetics
  • Trinucleotide Repeats / genetics