Inhibition of Jagged-mediated Notch signaling disrupts zebrafish biliary development and generates multi-organ defects compatible with an Alagille syndrome phenocopy

Development. 2004 Nov;131(22):5753-66. doi: 10.1242/dev.01411.

Abstract

The Alagille Syndrome (AGS) is a heritable disorder affecting the liver and other organs. Causative dominant mutations in human Jagged 1 have been identified in most AGS patients. Related organ defects occur in mice that carry jagged 1 and notch 2 mutations. Multiple jagged and notch genes are expressed in the developing zebrafish liver. Compound jagged and notch gene knockdowns alter zebrafish biliary, kidney, pancreatic, cardiac and craniofacial development in a manner compatible with an AGS phenocopy. These data confirm an evolutionarily conserved role for Notch signaling in vertebrate liver development, and support the zebrafish as a model system for diseases of the human biliary system.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Alagille Syndrome / embryology
  • Alagille Syndrome / metabolism*
  • Alagille Syndrome / pathology
  • Animals
  • Animals, Genetically Modified
  • Bile Ducts / embryology
  • Bile Ducts / metabolism
  • Biliary Tract / embryology*
  • Biliary Tract / metabolism*
  • Calcium-Binding Proteins / antagonists & inhibitors
  • Calcium-Binding Proteins / genetics
  • Calcium-Binding Proteins / metabolism*
  • Intercellular Signaling Peptides and Proteins
  • Jagged-1 Protein
  • Jagged-2 Protein
  • Ligands
  • Liver / anatomy & histology
  • Liver / cytology
  • Liver / embryology
  • Liver / metabolism
  • Mammals / anatomy & histology
  • Membrane Proteins / metabolism*
  • Microscopy, Electron, Transmission
  • Receptors, Notch
  • Serrate-Jagged Proteins
  • Signal Transduction*
  • Zebrafish / abnormalities
  • Zebrafish / embryology*
  • Zebrafish / metabolism
  • Zebrafish Proteins / antagonists & inhibitors
  • Zebrafish Proteins / genetics
  • Zebrafish Proteins / metabolism*

Substances

  • Calcium-Binding Proteins
  • Intercellular Signaling Peptides and Proteins
  • JAG1 protein, human
  • Jag1 protein, mouse
  • Jag3 protein, zebrafish
  • Jagged-1 Protein
  • Jagged-2 Protein
  • Ligands
  • Membrane Proteins
  • Receptors, Notch
  • Serrate-Jagged Proteins
  • Zebrafish Proteins
  • jag1a protein, zebrafish
  • jag2b protein, zebrafish