Efficacy of gene therapy for SCID is being confirmed

Lancet. 2004 Dec;364(9452):2155-6. doi: 10.1016/S0140-6736(04)17603-4.

Authors

Marina Cavazzana-Calvo¹, Alain Fischer

Affiliation

¹ Département de Biothérapie, Hôpital Necker-Enfants Malades, 75015 Paris, France. [email protected]

PMID: 15610783
DOI: 10.1016/S0140-6736(04)17603-4

No abstract available

Publication types

Comment

MeSH terms

Adenosine Deaminase / deficiency
Antigens, CD34 / analysis
Bone Marrow Cells / immunology
Bone Marrow Transplantation
Gammaretrovirus
Gene Transfer Techniques
Genetic Diseases, X-Linked / therapy*
Genetic Therapy* / adverse effects
Genetic Therapy* / methods
Genetic Vectors
Humans
Immunity, Cellular
Interleukin Receptor Common gamma Subunit
Receptors, Interleukin-7 / genetics
Severe Combined Immunodeficiency / genetics
Severe Combined Immunodeficiency / immunology
Severe Combined Immunodeficiency / therapy*
Transduction, Genetic

Substances

Antigens, CD34
IL2RG protein, human
Interleukin Receptor Common gamma Subunit
Receptors, Interleukin-7
Adenosine Deaminase