Development of novel therapies for Huntington's disease: hope and challenge

Acta Pharmacol Sin. 2005 Feb;26(2):129-42. doi: 10.1111/j.1745-7254.2005.00520.x.

Abstract

Huntington's disease (HD) is an autosomal dominant neurological disease. It is a fatal neurological disorder affecting 5-10 out of 10,000 people. While there are intensive research efforts focusing on uncovering molecular mechanisms of the pathogenesis of HD, a number of studies have begun to look for effective therapies for HD. There is a large body of encouraging news on novel therapeutic developments. The present paper reviews drugs used for symptomatic treatment of HD and experimental therapies targeting HD molecular pathology.

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Amantadine / therapeutic use
  • Animals
  • Cell Transplantation
  • Drugs, Chinese Herbal / therapeutic use
  • Humans
  • Huntingtin Protein
  • Huntington Disease / drug therapy*
  • Huntington Disease / genetics
  • Huntington Disease / therapy
  • Mutation
  • Neostriatum / cytology
  • Nerve Tissue Proteins / genetics*
  • Neuroprotective Agents / therapeutic use*
  • Nuclear Proteins / genetics*
  • Riluzole / therapeutic use

Substances

  • Drugs, Chinese Herbal
  • HTT protein, human
  • Huntingtin Protein
  • Nerve Tissue Proteins
  • Neuroprotective Agents
  • Nuclear Proteins
  • Riluzole
  • Amantadine