Gene therapy: the 'pro-sense' approach to Duchenne muscular dystrophy

Eur J Hum Genet. 2005 May;13(5):518-9. doi: 10.1038/sj.ejhg.5201381.
No abstract available

Publication types

  • News

MeSH terms

  • Animals
  • Dystrophin / biosynthesis
  • Dystrophin / genetics
  • Exons*
  • Genetic Therapy*
  • Humans
  • Mice
  • Muscular Dystrophy, Duchenne / genetics*
  • Muscular Dystrophy, Duchenne / therapy*
  • Oligoribonucleotides, Antisense / therapeutic use*
  • RNA, Small Nuclear / therapeutic use
  • Suppression, Genetic

Substances

  • Dystrophin
  • Oligoribonucleotides, Antisense
  • RNA, Small Nuclear