Long-term mixed chimerism after immunologic conditioning and MHC-mismatched stem-cell transplantation is dependent on NK-cell tolerance

Blood. 2005 Sep 15;106(6):2215-20. doi: 10.1182/blood-2005-04-1391. Epub 2005 May 31.

Abstract

T-cell tolerance is mandatory for major histocompatibility complex (MHC)-mismatched stem-cell transplantation without cytoreduction. Here, we used a cytotoxicity assay based on the infusion of differentially carboxyfluorescein succinimidyl ester (CFSE)-labeled syngeneic and donor splenocytes to determine the survival of donor cells in vivo. In vivo cytotoxicity data showed that treatment with anti-CD40 ligand monoclonal antibody in combination with a low dose of MHC-mismatched bone marrow cells was sufficient to induce T-cell tolerance. However, CFSE-labeled donor cells were still eliminated. A similar elimination pattern was observed in T-cell and natural killer T-cell (NKT-cell)-deficient mice, suggesting the involvement of natural killer (NK) cells. Indeed, in vivo NK-cell depletion resulted in a prolonged survival of CFSE-labeled donor cells, confirming the role of NK cells in this process. Transplantation of a megadose of MHC-mismatched bone marrow cells was required for a complete survival of CFSE-labeled donor cells. This NK-cell tolerance was donor specific and was associated with mixed chimerism. Additional NK-cell depletion significantly enhanced engraftment and allowed long-term chimerism after transplantation of a relatively low dose of donor bone marrow cells. These data demonstrate the importance of NK cells in the rejection of MHC-mismatched hematopoietic cells and may explain the high numbers of bone marrow cells required for transplantation over MHC barriers.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antibodies, Monoclonal / pharmacology
  • Antibodies, Monoclonal / therapeutic use
  • CD40 Ligand
  • Cytotoxicity, Immunologic
  • Graft Survival
  • Hematopoietic Stem Cell Transplantation / methods*
  • Histocompatibility Antigens
  • Histocompatibility*
  • Immune Tolerance* / drug effects
  • Immune Tolerance* / immunology
  • Killer Cells, Natural / immunology*
  • Mice
  • Mice, Inbred C57BL
  • Transplantation Chimera*
  • Transplantation Conditioning / methods*
  • Transplantation, Homologous

Substances

  • Antibodies, Monoclonal
  • Histocompatibility Antigens
  • CD40 Ligand