Three severe cases of EBS Dowling-Meara caused by missense and frameshift mutations in the keratin 14 gene

J Invest Dermatol. 2006 Apr;126(4):773-6. doi: 10.1038/sj.jid.5700154.

Abstract

We report three unrelated patients affected at birth with an unusually severe form of epidermolysis bullosa simplex Dowling-Meara type (EBS-DM) because of mutations in KRT14 encoding keratin 14. Two patients were heterozygous for the previously described p.M119T mutation. The third patient was heterozygous for a novel c.1246delC mutation predicting the replacement of the helix termination peptide and the tail domain by a 25 amino-acid aberrant carboxyterminal sequence. At age 2 years, patients carrying the p.M119T mutation still suffered from severe EBS-DM, whereas the patient harboring the c.1246delC mutation has improved over time. These cases illustrate genotype-phenotype correlations and have implications for genetic counselling of EBS.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child, Preschool
  • Epidermolysis Bullosa Simplex / genetics*
  • Epidermolysis Bullosa Simplex / pathology*
  • Frameshift Mutation
  • Humans
  • Infant
  • Keratin-14
  • Keratins / analysis
  • Keratins / genetics*
  • Keratins / metabolism
  • Male
  • Mutation, Missense
  • Skin / chemistry
  • Skin / ultrastructure

Substances

  • KRT14 protein, human
  • Keratin-14
  • Keratins