Characterization of an immuno 'stealth' derivative of the herpes simplex virus thymidine-kinase gene

Cancer Gene Ther. 2006 Jun;13(6):584-91. doi: 10.1038/sj.cgt.7700925.

Abstract

The cellular immune response against transgene-encoded neoantigens is a potential hurdle in gene therapy applications where long-term expression of transgenes is desired. Here a new optimized derivative of the herpes simplex virus 1-thymidine-kinase (HSV1-TK) gene is described. The HSV-TK gene is frequently used in experimental studies on gene-directed enzyme prodrug therapy. In the optimized gene, the HSV-TK coding region is fused with the codons for the Gly-Ala repeat of the Epstein-Barr virus nuclear-antigen 1 to prevent proteasomal degradation of the HSV-TK. To measure the protective effect in vitro, a model cytotoxic T lymphocyte epitope derived from the ovalbumin was inserted in the TK. Cells expressing the GAr-modified TK do not present TK-derived peptides in the major histocompatibility complex. Furthermore, conservative nucleotide substitutions were introduced, which prevent splicing, as well as mutations that render the TK-expressing cells more sensitive to ganciclovir (GCV). The GAr HSV-TK fusion protein is fully functional in vitro. This HSV-TK gene may be especially useful in those gene therapy applications where an immune response against the transgene-encoded product would frustrate the treatment.

MeSH terms

  • Antigen Presentation
  • Base Sequence
  • Cloning, Molecular
  • Epstein-Barr Virus Nuclear Antigens / genetics
  • Genetic Therapy / methods*
  • Genetic Vectors*
  • Humans
  • Molecular Sequence Data
  • Receptors, Immunologic / metabolism
  • Recombinant Fusion Proteins / genetics
  • Simplexvirus / enzymology*
  • T-Lymphocytes, Cytotoxic / metabolism
  • Thymidine Kinase / genetics*
  • Thymidine Kinase / immunology*

Substances

  • Epstein-Barr Virus Nuclear Antigens
  • Receptors, Immunologic
  • Recombinant Fusion Proteins
  • Thymidine Kinase
  • EBV-encoded nuclear antigen 1