Survival and function of intrastriatally grafted primary fibroblasts genetically modified to produce L-dopa

Neuron. 1991 Mar;6(3):371-80. doi: 10.1016/0896-6273(91)90246-v.

Abstract

A combination of gene transfer and intracerebral grafting may provide a powerful technique for examining the role of discrete substances in the development or functioning of the brain. In the present study, primary fibroblasts obtained from a skin biopsy from inbred Fischer rats were used as donor cells for genetic modification and grafting. When grafted to the striatum of Fischer rats with a prior 6-hydroxydopamine lesion, primary fibroblasts containing a transgene for either tyrosine hydroxylase (TH) or beta-galactosidase survived for 10 weeks and continued to express the transgene. TH synthesized by the implanted fibroblasts appeared to convert tyrosine to L-dopa actively, as observed in vitro, and to affect the host brain, as assessed through a behavioral measurement. These results suggest that primary fibroblasts genetically altered to express TH have the capacity to deliver L-dopa locally to the striatum in quantities sufficient to compensate partially for the loss of intrinsic striatal dopaminergic input.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Cell Survival / physiology
  • Fibroblasts / cytology*
  • Fibroblasts / metabolism
  • Fibroblasts / physiology
  • Levodopa / metabolism*
  • Rats
  • Rats, Inbred F344
  • Skin / cytology
  • Skin Transplantation / physiology
  • Transfection
  • Tyrosine 3-Monooxygenase / genetics
  • Tyrosine 3-Monooxygenase / metabolism
  • beta-Galactosidase / genetics
  • beta-Galactosidase / metabolism

Substances

  • Levodopa
  • Tyrosine 3-Monooxygenase
  • beta-Galactosidase