An inhibitor of serine proteases, neuroserpin, acts as a neuroprotective agent in a mouse model of neurodegenerative disease

J Neurosci. 2006 Oct 11;26(41):10614-9. doi: 10.1523/JNEUROSCI.3582-06.2006.

Abstract

Various studies suggest that proteolytic activity may be involved in a number of neurodegenerative disorders, including stroke and seizure. In this report, we examined the role of tryptic serine proteases, plasminogen activators (PAs), in the evolution of a neurodegenerative disease. Transgenic mice overexpressing an axonally secreted inhibitor of serine proteases (neuroserpin) were crossed with mice characterized by a "dying-back" motor neuron disease [progressive motor neuronopathy (pmn/pmn)]. Compared with pmn/pmn mice that showed an increase in PA activity, double mutant mice had decreased PA activity in sciatic nerves and spinal cord; their lifespan was increased by 50%, their motor behavior was stabilized, and histological analysis revealed increased numbers of myelinated axons and rescue of motoneuron number and size. This is the first report showing that a class of serine proteases (PAs) may be involved in the pathogenesis of a motor neuron disease and more specifically in axonal degeneration. Inhibiting serine proteases could offer a new strategy for delaying these disorders.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Disease Models, Animal*
  • Mice
  • Mice, Transgenic
  • Neurodegenerative Diseases / drug therapy
  • Neurodegenerative Diseases / enzymology*
  • Neuropeptides / biosynthesis*
  • Neuropeptides / therapeutic use
  • Neuroprotective Agents / metabolism*
  • Neuroprotective Agents / therapeutic use
  • Neuroserpin
  • Serine Endopeptidases / metabolism
  • Serine Proteinase Inhibitors / biosynthesis*
  • Serine Proteinase Inhibitors / therapeutic use
  • Serpins / biosynthesis*
  • Serpins / therapeutic use

Substances

  • Neuropeptides
  • Neuroprotective Agents
  • Serine Proteinase Inhibitors
  • Serpins
  • Serine Endopeptidases