Evaluation of pharmacokinetics, efficacy and safety of Immunate solvent detergent in previously treated patients with severe haemophilia A

Haemophilia. 2007 Jan;13(1):9-11. doi: 10.1111/j.1365-2516.2006.01412.x.

Abstract

Immunate Solvent Detergent (S/D) is a plasma derived, purified, human factor VIII (FVIII) - von Willebrand factor (VWF) complex subjected to two virus inactivation/removal processes: S/D and vapor heat treatment. This prospective, multicentre, three-part clinical study evaluated the pharmacokinetics (in comparison to the predecessor product Immunate), efficacy and safety of Immunate S/D in 56 previously treated patients with severe haemophilia A. Subjects received Immunate S/D on-demand, as a prophylactic regimen or both. The results of the pharmacokinetic population demonstrate that Immunate and Immunate S/D were equivalent with respect to the FVIII - and to the retrospectively VWF - parameters assessed. A total of 623 bleeding episodes were reported in 47/56 subjects. The duration of prophylaxis ranged from 0.1-5.2 months with a total of 175.6 months. The median number of bleeds per month in subjects on prophylaxis was 0 (range 0-10). Ninety-six percent of bleeding episodes were rated as having an excellent or good response. For most bleeding episodes (89%), subjects required only one infusion with a mean dose of 29.6 IU kg(-1). No FVIII inhibitory antibodies were observed in any subject. No related serious adverse events were reported. Thus, the introduction of S/D treatment did not alter the PK characteristics and function of VWF and FVIII molecules of Immunate S/D which is effective and safe for treatment of bleeding episodes, management of surgical procedures, and prophylaxis.

Publication types

  • Multicenter Study
  • Randomized Controlled Trial

MeSH terms

  • Detergents / adverse effects
  • Detergents / pharmacokinetics*
  • Factor VIII / pharmacokinetics*
  • Hemophilia A / blood
  • Hemophilia A / drug therapy*
  • Hemophilia A / virology
  • Hemorrhage / drug therapy
  • Hemorrhage / prevention & control
  • Humans
  • Pain / drug therapy
  • Pain / prevention & control
  • Prospective Studies
  • Safety
  • Solvents / adverse effects
  • Solvents / pharmacokinetics*
  • Treatment Outcome
  • Virus Inactivation

Substances

  • Detergents
  • Immunate solvent detergent, human
  • Solvents
  • Factor VIII