Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA

Adv Exp Med Biol. 2006:572:247-53. doi: 10.1007/0-387-32442-9_35.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Carrier Proteins / genetics
  • Electroretinography / methods
  • Eye Proteins / genetics
  • Genetic Therapy / methods*
  • Genetic Vectors*
  • Green Fluorescent Proteins / metabolism
  • Humans
  • Lentivirus / genetics*
  • Lentivirus / metabolism
  • Mice
  • Mice, Knockout
  • Optic Atrophy, Hereditary, Leber / genetics*
  • Optic Atrophy, Hereditary, Leber / therapy*
  • Pigment Epithelium of Eye / metabolism*
  • Promoter Regions, Genetic*
  • Retina / metabolism
  • cis-trans-Isomerases

Substances

  • Carrier Proteins
  • Eye Proteins
  • Green Fluorescent Proteins
  • retinoid isomerohydrolase
  • cis-trans-Isomerases