A new X-linked mental retardation (XLMR) syndrome with late-onset primary testicular failure, short stature and microcephaly maps to Xq25-q26

Eur J Med Genet. 2007 May-Jun;50(3):216-23. doi: 10.1016/j.ejmg.2007.01.003. Epub 2007 Jan 27.

Abstract

X-linked mental retardation (XLMR) is a heterogeneous disorder with both syndromic and non-syndromic forms. Here we describe the clinical and molecular characterisation of a family with a syndromic form of XLMR with hypogonadism and short stature. We investigated a family in which four male members in two generations presented with hypergonadotrophic hypogonadism associated with development of small and abnormal testes. In two of the males, late-onset testicular ascent was noted. In addition, all affected males had short stature (<0.4th centile) and mild learning difficulties and three out of the four had microcephaly. Karyotypes were normal and endocrine investigations confirmed primary testicular failure. The phenotype segregated as an X-linked trait. Haplotype and genetic two-point linkage analysis with 22 microsatellites excluded the whole X chromosome except for a region on Xq25-Xq27 encompassing 13.7Mb with a maximum LOD score of 1.1 for marker DXS8038 at theta=0.05. One family previously described as having XLMR with hypogonadism and short stature maps to the same X chromosome region implicated in our family. However, the more severe mental retardation, muscle wasting and tremor described in this other family would suggest that our family is affected by a novel XLMR syndrome.

Publication types

  • Case Reports

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Chromosome Mapping
  • Chromosomes, Human, X / genetics*
  • Facies
  • Female
  • Growth Disorders / complications
  • Growth Disorders / genetics*
  • Haplotypes
  • Humans
  • Hypogonadism / complications
  • Hypogonadism / genetics
  • Male
  • Mental Retardation, X-Linked / complications
  • Mental Retardation, X-Linked / genetics*
  • Mental Retardation, X-Linked / pathology
  • Microcephaly / complications
  • Microcephaly / genetics*
  • Microsatellite Repeats
  • Pedigree
  • Syndrome
  • Testicular Diseases / complications
  • Testicular Diseases / genetics*