Construction of diverse adeno-associated viral libraries for directed evolution of enhanced gene delivery vehicles

Nat Protoc. 2006;1(2):701-6. doi: 10.1038/nprot.2006.93.

Abstract

Rational design of improved gene delivery vehicles is a challenging and potentially time-consuming process. As an alternative approach, directed evolution can provide a rapid and efficient means for identifying novel proteins with improved function. Here we describe a methodology for generating very large, random adeno-associated viral (AAV) libraries that can be selected for a desired function. First, the AAV2 cap gene is amplified in an error-prone PCR reaction and further diversified through a staggered extension process. The resulting PCR product is then cloned into pSub2 to generate a diverse (>10(6)) AAV2 plasmid library. Finally, the AAV2 plasmid library is used to package a diverse pool of mutant AAV2 virions, such that particles are composed of a mutant AAV genome surrounded by the capsid proteins encoded in that genome, which can be used for functional screening and evolution. This procedure can be performed in approximately 2 weeks.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Cell Line
  • Dependovirus / genetics*
  • Directed Molecular Evolution / methods*
  • Gene Library*
  • Gene Targeting / methods
  • Genetic Therapy / methods
  • Genetic Vectors / genetics*
  • Genome, Viral
  • Humans
  • Mutagenesis
  • Plasmids / genetics
  • Transfection / methods