Development of an approach for ab initio estimation of compound-induced liver injury based on global gene transcriptional profiles

Genome Inform. 2006;17(2):77-88.

Abstract

Toxicity is a major cause of failure in drug development. A toxicogenomic approach may provide a powerful tool for better assessing the potential toxicity of drug candidates. Several approaches have been reported for predicting hepatotoxicity based on reference compounds with well-studied toxicity mechanisms. We developed a new approach for assessing compound-induced liver injury without prior knowledge of a compound's mechanism of toxicity. Using samples from rodents treated with 49 known liver toxins and 10 compounds without known liver toxicity, we derived a hepatotoxicity score as a single quantitative measurement for assessing the degree of induced liver damage. Combining the sensitivity of the hepatotoxicity score and the power of a machine learning algorithm, we then built a model to predict compound-induced liver injury based on 212 expression profiles. As estimated in an independent data set of 54 expression profiles, the built model predicted compound-induced liver damage with 90.9% sensitivity and 88.4% specificity. Our findings illustrate the feasibility of ab initio estimation of liver toxicity based on transcriptional profiles.

MeSH terms

  • Alanine Transaminase / blood
  • Algorithms
  • Animals
  • Artificial Intelligence
  • Aspartate Aminotransferases / blood
  • Bilirubin / blood
  • Chemistry, Clinical / methods
  • Cholesterol / blood
  • Cluster Analysis
  • Dose-Response Relationship, Drug
  • Drug-Related Side Effects and Adverse Reactions* / chemically induced
  • Drug-Related Side Effects and Adverse Reactions* / classification
  • Drug-Related Side Effects and Adverse Reactions* / metabolism
  • Feasibility Studies
  • Gene Expression Profiling*
  • Liver / drug effects*
  • Liver / enzymology
  • Liver / pathology
  • Models, Biological
  • Pharmaceutical Preparations / classification
  • Rats
  • Rats, Sprague-Dawley
  • Sensitivity and Specificity
  • Toxicogenetics / methods*
  • Transcription, Genetic*

Substances

  • Pharmaceutical Preparations
  • Cholesterol
  • Aspartate Aminotransferases
  • Alanine Transaminase
  • Bilirubin