Sample size estimation for non-inferiority trials of time-to-event data

Pharm Stat. 2008 Oct-Dec;7(4):236-44. doi: 10.1002/pst.292.

Abstract

We consider the problem of sample size calculation for non-inferiority based on the hazard ratio in time-to-event trials where overall study duration is fixed and subject enrollment is staggered with variable follow-up. An adaptation of previously developed formulae for the superiority framework is presented that specifically allows for effect reversal under the non-inferiority setting, and its consequent effect on variance. Empirical performance is assessed through a small simulation study, and an example based on an ongoing trial is presented. The formulae are straightforward to program and may prove a useful tool in planning trials of this type.

MeSH terms

  • Clinical Trials as Topic / methods*
  • Clinical Trials as Topic / standards
  • Clinical Trials as Topic / statistics & numerical data*
  • Follow-Up Studies
  • Humans
  • Research Design / standards
  • Sample Size*
  • Time Factors