A novel mutation in the PHF8 gene is associated with X-linked mental retardation with cleft lip/cleft palate

Clin Genet. 2007 Jul;72(1):19-22. doi: 10.1111/j.1399-0004.2007.00817.x.

Abstract

Recently, two truncating mutations in the PHF8 (plant homeodomain finger protein 8) gene have been found to cause X-linked mental retardation associated with cleft lip/cleft palate (CL/P). One of the truncating mutations was found in the original family with Siderius-Hamel CL/P syndrome where only two of the three affected individuals had mental retardation (MR) with CL/P and one individual had mild MR. The second mutation was present in a family with four affected men, three of whom had MR and CL/P, while the fourth individual had mild MR without clefting. Here, we report a novel nonsense mutation (p.K177X) in a male patient who has MR associated with CL/P. The mutation results in a truncated PHF8 protein lacking the Jumonji-like C terminus domain and five nuclear localization signals. Our finding further supports the hypothesis that the PHF8 protein may play an important role in cognitive function and midline formation.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural

MeSH terms

  • Adolescent
  • Adult
  • Alleles
  • Base Sequence
  • Cleft Lip / complications*
  • Cleft Lip / genetics*
  • Cleft Palate / complications*
  • Cleft Palate / genetics*
  • Codon, Nonsense*
  • DNA Primers / genetics
  • Exons
  • Female
  • Histone Demethylases
  • Humans
  • Male
  • Point Mutation
  • Syndrome
  • Transcription Factors / genetics*
  • X-Linked Intellectual Disability / complications*
  • X-Linked Intellectual Disability / genetics*

Substances

  • Codon, Nonsense
  • DNA Primers
  • Transcription Factors
  • Histone Demethylases
  • PHF8 protein, human