Detection of transaldolase deficiency by quantification of novel seven-carbon chain carbohydrate biomarkers in urine

J Inherit Metab Dis. 2007 Oct;30(5):735-42. doi: 10.1007/s10545-007-0590-2. Epub 2007 Jun 27.

Abstract

Transaldolase deficiency, a recently discovered disorder of carbohydrate metabolism with multisystem involvement, has been diagnosed in 6 patients. Affected patients have abnormal concentrations of polyols in body fluids and in all patients we have previously found increased amounts of a seven-carbon chain carbohydrate which we suspected of being sedoheptulose. We report development of a liquid chromatography-tandem mass spectrometry method for quantitation of the seven-carbon carbohydrates sedoheptulose and mannoheptulose in urine. Additionally, other seven-carbon chain carbohydrates were characterized in urine, including sedoheptitol, perseitol and sedoheptulose 7-phosphate. Transaldolase-deficient patients had significantly increased urinary sedoheptulose and sedoheptulose 7-phosphate, associated with subtle elevations of mannoheptulose, sedoheptitol and perseitol. Our findings reveal novel urinary biomarkers for identification of transaldolase deficiency.

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Biomarkers / urine
  • Carbohydrate Metabolism, Inborn Errors / diagnosis*
  • Carbohydrate Metabolism, Inborn Errors / enzymology
  • Carbohydrate Metabolism, Inborn Errors / genetics
  • Carbohydrate Metabolism, Inborn Errors / urine
  • Child
  • Child, Preschool
  • Chromatography, Liquid* / standards
  • Female
  • Heptoses / urine*
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Mannoheptulose / urine
  • Middle Aged
  • Reference Values
  • Reproducibility of Results
  • Sugar Phosphates / urine
  • Tandem Mass Spectrometry* / standards
  • Transaldolase / deficiency*
  • Transaldolase / genetics
  • Urinalysis / methods*
  • Urinalysis / standards

Substances

  • Biomarkers
  • Heptoses
  • Sugar Phosphates
  • sedoheptulose 7-phosphate
  • sedoheptulose
  • perseitol
  • Mannoheptulose
  • Transaldolase